Adeno-associated virus (AAV)-mediated RNA interference to PABPN1 combined with an optimised resistant transgene for rescue of the muscle specific disease oculopharyngeal muscular dystrophy (OPMD)
Houria Bachtarzi, Alberto Malerba, Susan Jarmin, Capucine Trollet, Michael Graham, George Dickson
Research output: Contribution to conference › Abstract
Fingerprint
Dive into the research topics of 'Adeno-associated virus (AAV)-mediated RNA interference to PABPN1 combined with an optimised resistant transgene for rescue of the muscle specific disease oculopharyngeal muscular dystrophy (OPMD)'. Together they form a unique fingerprint.